The knowledge base

Steven Axon is the CEO of Prothelia, a biopharmaceutical company based in Massachusetts, USA, committed to developing a promising new…

Professor Bert Smeets is involved in a number of investigations looking into a muscle stem cell treatment strategy to treat…

The Congenital Muscle Disease International Registry (CMDIR) aims to advance neuromuscular research by collecting vital data and by growing advocacy…

Drs. Karlijn Bouman (PhD Candidate) is part of a team of Dutch doctors and researchers that are carrying out a…

Dr. Carsten Bönnemann and Dr. Reghan Foley are running a natural history study for infants aged 0-5 years of age.…

As a respiratory therapist and an innovator, Ruud van der Wel has been able to develop amazing tools that can…