The knowledge base

Meet Justin: an exceptional young man who, despite living with the LAMA2-CMD, has been living his life to the fullest…

The collaboration between the three European patient organizations (Voor Sara, ImpulsaT and Lama2 France) has been formalized and has led…

The following is an interview with Sandy who lives with a severe form of LAMA2-CMD. Hello Sandy, could you present…

This week has seen the roll out of the new and updated version of the MDC1A.com website! Continuing our efforts…

Dr. Yurchenco (NJ, USA) and Dr. Rüegg (Basel, Switzerland) are collaborating with Santhera Pharmaceuticals to develop an emerging gene therapy…

The Generate Your Muscle (GYM) project was recently set up with the aim of developing and commercialising affordable stem cell…