The knowledge base

This month, Maastricht UMC, led by Professor Bert Smeets, started a first clinical study in which healthy stem cells from…

Muscles On Wheels: a children’s book about a girl in a wheelchair! We will soon be able to finish and…

Meet Justin: an exceptional young man who, despite living with the LAMA2-CMD, has been living his life to the fullest…

The collaboration between the three European patient organizations (Voor Sara, ImpulsaT and Lama2 France) has been formalized and has led…

The following is an interview with Sandy who lives with a severe form of LAMA2-CMD. Hello Sandy, could you present…

This week has seen the roll out of the new and updated version of the MDC1A.com website! Continuing our efforts…