
Dr Kemaladewi secures vital funding to advance LAMA2-CMD gene therapy research
Dr. Dwi Kemaladewi and her team at the University of Pittsburgh have been diligently working on the development of a…
Our mission is to further advance awareness and research for LAMA2-CMD internationally and to directly support patients and families by providing relevant information and resources.
This website brings together the international LAMA2-CMD community and centralises all information, education, community news and research and industry updates directly relating to the fight against LAMA2-CMD.
By including the patients and families, and by collaborating with the clinicians, researchers and members of the biotech industry involved with LAMA2-CMD around the world, we aim to accelerate the road to therapy in a truly united and collective global effort.
Find more on our objectives and who we are here.
Patient Organisation
Founded by the parents of Marko in 2023, LAMA2 Bulgaria aims to accelerate the path to clinical trials by connecting affected families in Bulgaria.
Find more information here.
Who: Dr. Francina Munell and Dr. Jordi Barquinero
Where: Barcelona, Spain
Research: Diagnostics and stem cell therapy for LAMA2-CMD patients
Dr. Dwi Kemaladewi and her team at the University of Pittsburgh have been diligently working on the development of a…
In september 2023 we started with the LAMA2-MD consortium meetings for researchers, clinicians, companies and patients and their representatives. The…
Professor Dr Madeleine Durbeej of Lund University, Sweden provided an overview of existing research on the mechanisms of LAMA2-CMD and…
On the 17-19th of March 2023 doctors, researchers, patients and families gathered in Barcelona for the second international conference on…
This month, Maastricht UMC, led by Professor Bert Smeets, started a first clinical study in which healthy stem cells from…
Hello everyone, From 17 till 19 March there will be an international conference about Lama2-MD in Barcelona. The conference LAMA2…
Muscles On Wheels: a children’s book about a girl in a wheelchair! This special story is written by three students…
Meet Justin: an exceptional young man who, despite living with the LAMA2-CMD, has been living his life to the fullest…
Dr. Avencia Sanchez-Mejías has been investigating how haematopoietic stem cells from LAMA2-CMD patients’ bone marrow, can be genetically corrected to…
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